Spectrum

February 2010

Strategic Overview of the Targeted Cancer Therapies Marketplace

Report Authors
Barbara M. Bolten, M.S., M.B.A.
Matthew Drapeau
Neil Grubert, M.A.
Lulu Pickering, Ph.D.
Prachi Vora, M.P.H.
George S. Mack, D.M.D.

Introduction:

The allure of blockbuster revenues, like those earned by Roche/Chugai’s targeted cancer drugs Avastin, Herceptin, and Rituxan/MabThera—each of which pulled in nearly $5 billion in 2008—makes this an attractive marketplace. The success of targeted cancer therapies signaled a paradigm shift in cancer treatment and launched a whole new industry. In today’s targeted cancer therapies marketplace, competitors are many, the pipeline is full, innovative R&D is flourishing, and unmet needs abound. Future success stories are likely as companies tap opportunities presented by unmet treatment needs, novel targets, premium pricing, companion diagnostics, and personalized medicine. At the same time, they must prepare to successfully navigate such challenges as the emergence of biosimilars, the cost and reimbursement pressures that will be brought to bear on premium-priced targeted cancer therapies, and increasing competition.

Questions Answered in This Report:

  *   The 2008 market for targeted oncology therapies was approximately $25 billion. Who are the major players in this market? What will be the value of this market in 2015, and what companies are the likely future leaders? What agents are in the clinical pipeline and how advanced are they? Which targeted therapies now in the pipeline that will launch before 2015 do Decision Resources Pharmaview analysts believe will have worldwide sales in excess of $500 million?

  *   In the 12-month period from November 2008 through October 2009, approximately 400 deals were executed in the oncology therapy area. What deals involved targeted therapies? What major mergers and acquisitions took place? Which product opportunities were inlicensed? What trends are developing in oncology dealmaking?

  *   Healthcare payers around the world have very different approaches to cost sharing for targeted cancer therapies. In the United States, how do commercial and Medicare health plans differ in their cost-sharing strategies? To what extent are European and Japanese patients required to contribute to their treatment costs? What impact does cost sharing have on patient access to targeted therapies?

  *   The influence of biomarkers in oncology has extended to just about every aspect of the drug-diagnostic relationship in the therapeutic area. How have biomarker-based tests performed in the marketplace? How are companies using biomarkers in clinical trials? What companies are leaders in biomarker development and dealmaking? How can diagnostics companies capitalize on pharma’s interest in diagnostic-therapeutic partnerships in the quest to make the preclinical and clinical development processes more efficient?

  *   Biotech companies are a rich source of innovation for the identification of novel targets and the development of new cancer therapeutics. Which companies have contributed targeted cancer drugs to the development pipeline? Which companies have innovative technologies for drug target and lead identification? Which companies are attracting the interest of Big Pharma for acquisition or collaboration?

  *   Companies developing new targeted cancer therapies will have to compete with today’s existing, very successful agents. What are the remaining unmet needs in this marketplace? How can companies differentiate their agents? What truly novel possibilities are in the works? What challenges should companies prepare to meet?

Scope:

Markets covered: United States, France, Germany, Italy, Spain, United Kingdom, Japan.

Diseases included: Actinic keratosis, basal cell carcinoma, breast cancer, chronic myelogenous leukemia (CML), colon cancer, colorectal cancer (CRC), erythema nodosum leprosum, esophageal cancer, gastrointestinal stromal tumors (GISTs), glioma, glioblastoma multiforme, head and neck cancer, hormone-refractory prostate cancer, thyroid cancer, melanoma, multiple myeloma, myelodysplastic syndromes, non-Hodgkin’s lymphoma, non-small-cell lung cancer (NSCLC), osteosarcoma, ovarian cancer, pancreatic cancer, prostate cancer, renal cell carcinoma (RCC), sarcoma.

Primary research – oncologists’ insights: Incorporates findings from a new survey of 224 U.S. oncologists regarding treatment patterns, unmet needs in oncology, cost and affordability of targeted therapies, prospects for increased cost-containment, receptiveness to the potential introduction of biosimilars, the role of biomarkers and companion diagnostics, and remaining opportunities for new targeted therapies.

Primary research – formulary data: comprehensive national data from Fingertip Formulary on formulary positioning and prescribing restrictions for 16 targeted therapies in commercial and Medicare plans.

Primary research – deals analysis: compilation and assessment of approximately 400 deals related to targeted cancer therapies including most activity companies, deal types, deal targets.

Decision Resources analyst insights: high-level Decision Resources custom epidemiology data from PatientBase; market sizing from Decision Resources Pharmaview; insights from analysts working in Decision Resources Spectrum, Pharmaview, New Products, and oncology therapeutic area.

International price comparison: comparative analysis of the prices of leading targeted cancer therapies in the United States, France, Germany, Italy, Spain, the United Kingdom, and Japan.

Reimbursement issues: formulary positioning, cost controls, health technology assessment, comparative effectiveness research, prescribing restrictions, Medicare, drug registries, distribution controls, hospital coverage, patient access schemes, National Institute for Health and Clinical Excellence, NICE.

Clinical pipeline: by phase, drug target, target indication, company type, company.

Drug targets: Epidermal growth factor receptor-2 (HER-2), tyrosine kinase, threonine protease, poly ADP-ribose polymerase (PARP), proteasome, glycoprotein NMB (GPNMB or osteoactivin), lipid kinases, NOD-2 receptor, phosphoinositide-3 kinase (PI3K), receptor tyrosine kinase MET, vascular endothelial growth factor receptor 2 (VEGFR2), receptor tyrosine kinase RET, mitogen-activated ERK kinase (MEK), receptor activator of nuclear factor κB (RANK), serine/threonine kinase RAF, multitargeted kinase inhibitors, signal transduction pathways, angiogenesis, pathways regulating cellular proliferation, growth, survival, differentiation, Philadelphia chromosome, histone modification, the proteasome, immune cells, apoptotic pathways, molecular chaperones.

Companies: profiles of current market leaders, pipeline leaders, leading innovator companies.

Spectrum Expert Commentary: George S. Mack, D.M.D., describes the irresistible value of using biomarkers in drug development and discusses key opportunities on the horizon.

Search Reports

Mentioned in this report:

  • - A*STAR
  • - Abbott Laboratories
  • - Ablynx
  • - Abraxis BioScience
  • - Agendia
  • - Allostera
  • - Almac Diagnostics
  • - American Cancer Society
  • - Amgen
  • - Ardea Biosciences
  • - Ariad Pharmaceuticals
  • - ArQule
  • - Array BioPharma
  • - Astellas Pharma
  • - Astex Therapeutics
  • - AstraZeneca
  • - Asuragen
  • - Attenuon
  • - Aveo Pharmaceuticals
  • - Bayer Healthcare
  • - Beckman Coulter
  • - Biogen Idec
  • - BioGenex
  • - BioInvent
  • - Biomerica
  • - bioMerieux
  • - Biomira Diagnostics
  • - BiPar Sciences
  • - Boehringer Ingelheim
  • - Brahms
  • - Bristol
  • - BTG
  • - Cancer Research Technology
  • - Cell Therapeutics
  • - Celldex Therapeutics
  • - Celleron Therapeutics
  • - Centocor (J&J)
  • - Champions Biotechnology
  • - ChemGenex Pharmaceuticals
  • - Chugai
  • - Clarient
  • - Claris Diagnostics
  • - Clinical Data
  • - Compugen
  • - CuraGen
  • - Curis
  • - Cyclacel
  • - Daiichi Sankyo
  • - Dako
  • - Dana
  • - Debiopharm
  • - DiagnoCure
  • - Diagnostic Systems Laboratories
  • - DxS
  • - Dyax
  • - Eisai
  • - Eli Lilly
  • - Enzon Pharmaceuticals
  • - Epigenomics
  • - Epistem
  • - Erimos Pharmaceuticals
  • - Exelixis
  • - Exosome Diagnostics
  • - Fujirebio Diagnostics
  • - Genentech
  • - General Electric
  • - GenMab
  • - Genomic Health
  • - GENova Biotherapeutics
  • - Genta
  • - Genzyme
  • - GlaxoSmithKline
  • - GlobeImmune
  • - Gloucester Pharmaceuticals
  • - H. Lee Moffitt Cancer Center
  • - Health Discovery
  • - Horizon Discovery
  • - Human Genome Sciences
  • - IDM Pharma
  • - ImClone Systems
  • - ImmunoCellular Therapeutics
  • - Immunogen
  • - Immunomedics
  • - Incyte
  • - Indiana University
  • - Infinity Pharmaceuticals
  • - Invitrogen
  • - Ipsen
  • - Isis Pharmaceuticals
  • - Janssen (J&J)
  • - Johns Hopkins University
  • - Johnson & Johnson
  • - KMI Diagnostics
  • - Kosan Biosciences
  • - Kronus
  • - KuDOS Pharmaceuticals
  • - Kyowa Hakko Kirin
  • - Lab21
  • - LEO Pharma
  • - Lonza
  • - Matritech
  • - MD Anderson Cancer Center
  • - Medarex
  • - MedImmune
  • - Merck & Co.
  • - Merrimack Pharmaceuticals
  • - Micromet
  • - Millennium Pharmaceuticals (Takeda)
  • - Molecular Logix
  • - Morphotek
  • - Mundipharma International
  • - Myriad Genetics
  • - Myriad Pharmaceuticals
  • - National Cancer Institute
  • - National Comprehensive Cancer Network (NCCN)
  • - National Health Service (U.K.)
  • - National Institute for Health and Clinical Excellence (NICE)
  • - Nerviano Medical Sciences
  • - Novartis
  • - Nuvera Biosciences
  • - Onconova Therapeutics
  • - Ontario Cancer Institute
  • - Onyx Pharmaceuticals
  • - Ortho (J&J)
  • - OSI Pharmaceuticals
  • - Oxford Biotherapeutics
  • - Peplin
  • - Pfizer
  • - PGxHealth
  • - Pharmacia (Pfizer)
  • - Pharmacyclics
  • - Piramed (Roche)
  • - Plexxikon
  • - Polymedco
  • - Predictive Biosciences
  • - PrognosDx Health
  • - Proteolix
  • - Qiagen
  • - Quest Diagnostics
  • - Regeneron
  • - Roche
  • - S*BIO
  • - SABiosciences
  • - Sanofi
  • - Santaris Pharma
  • - Scantibodies Laboratory
  • - Schering (Merck)
  • - Seattle Genetics
  • - Serenex
  • - Servier
  • - Siemens Healthcare Diagnostics
  • - Spectrum Pharmaceuticals
  • - St. Gallen International Consensus Panel
  • - Supergen
  • - Synta Pharmaceuticals
  • - Takeda
  • - TAP
  • - Thrombogenics
  • - TopoTarget
  • - Tosoh Bioscience
  • - Tracon Pharmaceuticals
  • - UC Los Angeles
  • - United Biotech
  • - University Hospital of Parma
  • - Veridex
  • - Vernalis
  • - Vertex Pharmaceuticals
  • - ViennaLab
  • - Vysis
  • - Wyeth (Pfizer)
  • - Yakult Honsha